Transform Cystic Fibrosis Treatment
Effective and accessible cystic fibrosis treatments through a personalized approach
Cystic Fibrosis (CF) is a rare, progressive genetic disorder affecting approximately 160,000 people worldwide. It leads to severe damage in the lungs, digestive system, and other vital organs.
CF is caused by mutations in the CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) gene, which impairs the function of the CFTR protein throughout the body. Over 2,000 different mutations of the CFTR gene have been identified to date.
Since 2012 effective modulator therapies have been introduced to correct the CFTR protein, but a significant part of people with CF are still unable to benefit from these therapies.
Our mission is to transform treatment for people living with cystic fibrosis by developing an innovative and accessible personalized treatment approach
Our vision is a world where cystic fibrosis is no longer a life-limiting condition, and every person living with this disease has equal access to effective and economically sustainable treatments
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